Tag Archives: dmd

January, 2016

November, 2015

  • 25 November

    FDA Panel Says BioMarin DMD Drug Data Not Persuasive

    SAN RAFAEL, Calif., Nov. 24, 2015 (GLOBE NEWSWIRE) — BioMarin Pharmaceutical Inc. (Nasdaq:BMRN) announced today that the Peripheral and Central Nervous System Drugs Advisory Committee of the U.S. Food and Drug Administration (FDA) met to discuss the data submitted to support the New Drug Application (NDA) for KyndrisaTM (drisapersen) for …

October, 2015

June, 2015

May, 2015

January, 2015

  • 27 January

    Scientists Use Modified RNA for Telomere Extension

    Scientists discovered a new procedure that can quickly and efficiently increase the length of human telomeres, which could help in a range of diseases, including Duchenne muscular dystrophy (DMD) to diabetes. Researchers from the Stanford University School of Medicine used modified messenger RNA to extend telomeres, the protective caps on …