Specialty Pharma Journal Specialty, Precision & Technology
SAN RAFAEL, Calif., March 21, 2016 (GLOBE NEWSWIRE) — BioMarin announced today that the pivotal Phase 3 PRISM-2 study (formerly referred to as 165-302) of pegvaliase met the primary endpoint of change in blood Phe compared with placebo (p<0.0001) in preliminary results. During the 8 week PRISM-2 double-blind, placebo-controlled, randomized …
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